Added: Jul 20, 2008
From: sciencentral
Duration: 1:28
As an 8-year-old boy becomes the first U.S. gene therapy patient for muscular dystrophy, one of the researchers behind the therapy talks about the 20 years it took to get there, and what lies in the future. Watch this ScienCentral video for more.
Channel: Howto
Tags: dystrophy gene genetic health muscular research science therapy
Rating: 4.40 (10 ratings) Views: 10853' favoriteCount='40 Comments: 35
blee20 Says:
Jul 20, 2008 - I myself have Limb Girdle Muscular Dystrophy and i am happy to see this
MolitvaSrb Says:
Jul 20, 2008 - Hey I have a question I also have MD I dunno what cinde of it is, and I like to know can we drink alcohol my dad dont let me drink coz 1 doctor sad people like me sould not drink coz it make us even weaker, but I [personaly think we should drink coz our life is shit, and drinking make us hapy, like evry 1 els who have a bad live , and im drunk atm
MolitvaSrb Says:
Jul 20, 2008 - im getting sober and im beginnig to think waht i sad is cuite dumb but i like tio drink, i have 20 years and i can still waljk i know i never gonna have girlfriend and i am n00b, i also think i have social anxiety disorder coz im afarid to talk to people, or maybie am just spoiled kid!!!!!
MolitvaSrb Says:
Jul 20, 2008 - quite dumb*
zaction Says:
Jul 20, 2008 - Dumb!? That's mature. I am doing some collaboration with Xiao Xiao and the man is no dummy. My boss is Qi Long Lu and he is world renowned in DMD and LGMD research. Maybe you could tell me why you think it is dumb?
zaction Says:
Jul 20, 2008 - Hello! I am working hard on LGMD and really feel there is great hope for treatment. My lab was started by a very wealthy man who's granddaughter has LGMD. Do you know which mutation you have in your FKRP gene? I can find the latest info for you if you like. Sincerely, Allen
zaction Says:
Jul 20, 2008 - Bless all of you folks who suffer. I am working hard on the disease and feel good that we will fins treatments for the numerous versions of DMD, LGMD, BMD, etc. I just got back from a gene therapy conference in Seattle Wash. and LOTS of progress if being made. Please hold on to hope.
greatbritain2k3 Says:
Jul 20, 2008 - molitva was correcting the spelling of a part of his previous post (although there were a lot of other spelling mistakes in it)
rambohs Says:
Jul 20, 2008 - Have A FEW jars man. I have many friends with MD LIKE ME AND IT DOES YOU NO HARM AT ALL. it's you life.
chelas00 Says:
Jul 20, 2008 - Hey zaction, I also have LGMD 2D, do you know where i can find the latest news or updates about my disease. How far do yo see stem cell therapy
historyforamir Says:
Jul 20, 2008 - Hi I have BMD, I am 17, and i am about to lose the ability to walk in few months.I think of alcohol too, but i believe it will wreck my life , so i sholud handle all the difficulties without alcohol.DONT DRINK, BROTHER!!!!!
historyforamir Says:
Jul 20, 2008 - Hi! i have BMD, i am 17 years old,i am about to lose the ability to walk soon.Can you give some advise about treatment. now i only take Steroids (prednisone), Creatine and Glutamine. This helps but Steroids are quite harmfull.Tell me what can i do??? !!!
zaction Says:
Jul 20, 2008 - Hello! You have a very strong will and a good attitude. This is the best thing you can do to be honest. Having a good outlook can work more wonders than any drug can. As far as treatments go, I am not a doc, so I can't really comment as I am not qualified to make those kind of assesments. Creatine, I hear is a good option. We are learning so much and will find help in the near future I feel. Hang on! :)
proguitarplayer2005 Says:
Jul 20, 2008 - Hi my mom has MD i might get it to we dont know yet im 13 and still dont have it i hope i never do but please tell me if theres a cure soon i mean i might die from the disease
roidroid Says:
Jul 20, 2008 - this is amazing, one injection will be able to make you glow green.this would be a good prank to pull on someone, and raise awareness of the power of gene therapy.
Genetherapynet Says:
Jul 20, 2008 - Very nice, hopefully it will work for a long time.Check more gene therapy news at Gene Therapy Net
jcishere08 Says:
Jul 20, 2008 - well I can say that the video is lying about MD. Because I have it and Im 27 years old. People with MD DO NOT LIVE UP TO 25!!! I myself am living proof of the matter!
CapriceK Says:
Jul 20, 2008 - yeah, the oldest guy was 55! I knew a guy who made it to 40. I'm 21 and my brother is 23, and we're still pretty mobile, both in wheelchairs but can still lean forward unassisted and stuff. Not even on oxygen or anything. Kind of at the stage most 13-14 year olds get. I did get cardiomyopathy last year but that's levelled out now.
zaction Says:
Jul 20, 2008 - It's called the EGFP gene (Enhanced Green Fluorescent Protein) Pretty cool :) I have worked with it a lot. Also, have worked with the guy mentioned here. Xiao Xiao. Very cutting edge stuff. I have been working on AON therapy for DMD. It has great potential. It works in the MdxE23 mouse. (Exon 23 mutation). I have developed DNA vectors for other exons (human ones). Exon 43,45,50,51,53. I hope these are a huge help some day.
zaction Says:
Jul 20, 2008 - Also check out the ASGT site for news
roidroid Says:
Jul 20, 2008 - the video says "usually" die by the age of 25.there's no lie
jcishere08 Says:
Jul 20, 2008 - i have known many ppl that r over 25 and ok.
jcishere08 Says:
Jul 20, 2008 - sweet
F1RE2WATER Says:
Jul 20, 2008 - Were the results positive?
Freakbox Says:
Jul 20, 2008 - I noticed this video is now a bit old.I am frustrated why this has not already been worked out.. and rediculous wars (and money for wars) take priority in US. Antisense? virus transport methods for carrying healing genes?Thx for vid anyhow- very intrsting.